Gene Therapy for Leber’s Disease

Gene Therapy recreates loss vision in children suffering from Leber’s Disease. [...]

Leber’s Disease – Gene therapy transforms eyesight

Pennsylvania researchers using gene therapy have made significant improvements in vision in 12 patients with a rare inherited visual defect, a finding that suggests it may be possible to produce similar improvements in a much larger number of patients with retinitis pigmentosa and macular degeneration. [...]